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信使核酸药物
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messenger nucleic acid drug
信使核酸药物
通过病毒或非病毒的方式(如电穿孔、基因枪、脂质体等)将体外合成的特定信使核糖核酸(mRNA)导入患者体内,通过翻译修饰,快速表达治疗所需具有药理活性的目标蛋白质,从而治疗某种疾病的药物。
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