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Mendelian disease
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Mendelian disease
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临床试验的自适应性设计
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Mendelian disease
孟德尔疾病
由一对等位基因控制、单个基因发生突变就足以发病的一类遗传性疾病,其传递方式遵循孟德尔分离定律。又称单基因疾病。
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