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依库珠单抗
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eculizumab
依库珠单抗
一种人源化的补体末端抑制型单克隆抗体,抑制补体介导的血细胞损伤,用于治疗两种罕见的基因突变型血液病:阵发性睡眠性血红蛋白尿症(paroxysmal nocturnal hemoglobinuria; PNH)和非典型溶血性尿毒症(atypical haemolytic uraemic syndrome; aHUS)。别称依库丽单抗、艾库组单抗。
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